Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001929292 | SCV002206824 | pathogenic | Leber congenital amaurosis 9 | 2022-06-27 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant disrupts a region of the NMNAT1 protein in which other variant(s) (p.Arg66Trp) have been determined to be pathogenic (PMID: 22842227, 24791140, 26018082, 28453600). This suggests that this is a clinically significant region of the protein, and that variants that disrupt it are likely to be disease-causing. This variant has not been reported in the literature in individuals affected with NMNAT1-related conditions. This variant is a gross deletion of the genomic region encompassing exon(s) 3-4 of the NMNAT1 gene. This variant would be expected to be in-frame, preserving the integrity of the reading frame. |