Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001980096 | SCV002227073 | uncertain significance | Frontotemporal dementia and/or amyotrophic lateral sclerosis 1; Paget disease of bone 2, early-onset | 2022-08-23 | criteria provided, single submitter | clinical testing | In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. This variant disrupts a region of the SQSTM1 protein in which other variant(s) (p.Ala381Val) have been observed in individuals with SQSTM1-related conditions (PMID: 17129171, 24042580). This suggests that this is a clinically significant region of the protein, and that variants that disrupt it are likely to be disease-causing. This variant has not been reported in the literature in individuals affected with SQSTM1-related conditions. This variant is a gross deletion of the genomic region encompassing exon(s) 6-7 of the SQSTM1 gene. This variant would be expected to be in-frame, preserving the integrity of the reading frame. |