Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Invitae | RCV004583471 | SCV005064577 | likely pathogenic | Zellweger spectrum disorders | 2019-12-21 | criteria provided, single submitter | clinical testing | In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. Loss-of-function variants in PEX1 are known to be pathogenic (PMID: 9398847, 16086329, 16141001, 21031596). This variant has not been reported in the literature in individuals with PEX1-related conditions. This variant is a deletion of the genomic region encompassing exon 4 and part of exon 5 (c.357+199_1167del) of the PEX1 gene. It is expected to disrupt RNA splicing and likely results in an absent or disrupted protein product. |