Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001031099 | SCV001194405 | likely pathogenic | Citrullinemia type I | 2019-06-10 | criteria provided, single submitter | clinical testing | This variant is an in-frame deletion of the genomic region encompassing exons 11-12 of the ASS1 gene. It preserves the integrity of the reading frame. Deletions of exons 11-12 have been observed in individuals affected with citrullinemia type 1 (PMID: 22494545, 19006241). This variant disrupts the p.Val263 amino acid residue in ASS1. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 14680976, 18473344, 21244552, 23780642, 18925679). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |