Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003782629 | SCV004604397 | pathogenic | Niemann-Pick disease, type B; Niemann-Pick disease, type A | 2023-12-21 | criteria provided, single submitter | clinical testing | This variant results in the deletion of part of exon 1 (c.-378_286del) of the SMPD1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in SMPD1 are known to be pathogenic (PMID: 12369017, 15221801). This variant is not present in population databases (gnomAD no frequency). This variant has not been reported in the literature in individuals affected with SMPD1-related conditions. For these reasons, this variant has been classified as Pathogenic. |