Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Pangenia Genomics, |
RCV003226005 | SCV003919731 | pathogenic | Charcot-Marie-Tooth disease, type IA | 2022-10-14 | criteria provided, single submitter | research | A copy number gain (copy number = 3) of the genomic region encompassing the full coding sequence of the PMP22 gene has been identified. Duplications of the region on chromosome 17p11.2 which contain the PMP22 gene cause Charcot-Marie-Tooth disease type 1A (CMT1A) (PMID: 1677316, 1822787). These reported duplications have been shown to lead to increased gene dosage as the functional defect in patients with CMT1A (PMID: 1303230). It has also been observed to segregate with disease in related individuals. |