Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001997197 | SCV002229689 | pathogenic | Severe neonatal-onset encephalopathy with microcephaly | 2021-07-16 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant disrupts the C-terminus of the MECP2 protein. Other variant(s) that disrupt this region have been determined to be pathogenic (PMID: 23696494, 10814718, 19914908, 16473305). This suggests that variants that disrupt this region of the protein are likely to be causative of disease. Nucleotide substitutions within the consensus splice site are a relatively common cause of aberrant splicing (PMID: 17576681, 9536098). Similar partial deletions have been reported in individuals with Rett syndrome (PMID: 14974082). This variant results in the deletion of exon(s) 3 and part of exon 4 (c.27-3848_1171del) of the MECP2 gene. While this variant is not anticipated to result in nonsense mediated decay, it likely alters RNA splicing and results in a disrupted protein product. |