Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Eurofins Ntd Llc |
RCV000179236 | SCV000231452 | likely pathogenic | not provided | 2015-02-04 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000779680 | SCV000916408 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2017-09-28 | criteria provided, single submitter | clinical testing | Variant summary: The ACAT1 c.455G>C (p.Gly152Ala) variant involves the alteration of a conserved nucleotide located in the buried Nbeta4 near an active site (Fukao_2002) and 4/4 in silico tools predict a damaging outcome for this variant (SNPsandGO not captured due to low reliability index). Functional studies support these predictions observing the variant to affect protein folding and/or dimerization but also accumulated unstable mutant protein (Fukao_2002 and Zhang_2004). This variant was found in 14/246162 control chromosomes at a frequency of 0.0000569, which does not exceed the estimated maximal expected allele frequency of a pathogenic ACAT1 variant (0.0028868). Multiple publications cite the variant in affected compound heterozygote patients. In addition, a clinical diagnostic laboratory classified this variant as likely pathogenic. Taken together, this variant is classified as pathogenic. |
Department of Pediatrics, |
RCV000779680 | SCV000966059 | likely pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2019-05-05 | criteria provided, single submitter | research | |
Labcorp Genetics |
RCV000779680 | SCV002242091 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2023-12-22 | criteria provided, single submitter | clinical testing | This sequence change replaces glycine, which is neutral and non-polar, with alanine, which is neutral and non-polar, at codon 152 of the ACAT1 protein (p.Gly152Ala). This variant is present in population databases (rs762991875, gnomAD 0.03%). This missense change has been observed in individual(s) with beta-ketothiolase deficiency (PMID: 7749408, 15128923, 28255778). ClinVar contains an entry for this variant (Variation ID: 198029). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ACAT1 protein function with a positive predictive value of 95%. Experimental studies have shown that this missense change affects ACAT1 function (PMID: 7749408, 15128923). For these reasons, this variant has been classified as Pathogenic. |
Fulgent Genetics, |
RCV000779680 | SCV002812842 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2022-03-08 | criteria provided, single submitter | clinical testing | |
Baylor Genetics | RCV000779680 | SCV004212861 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2024-03-19 | criteria provided, single submitter | clinical testing |