Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Department of Pediatrics, |
RCV000844795 | SCV000966068 | likely pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2019-05-05 | criteria provided, single submitter | research | |
Labcorp Genetics |
RCV000844795 | SCV001217723 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2023-05-31 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Experimental studies have shown that this missense change affects ACAT1 function (PMID: 27928777). An algorithm developed to predict the effect of missense changes on protein structure and function (PolyPhen-2) suggests that this variant is likely to be disruptive. ClinVar contains an entry for this variant (Variation ID: 666490). This missense change has been observed in individual(s) with beta-ketothiolase deficiency (PMID: 23958592, 27928777). This variant is present in population databases (rs541517496, gnomAD 0.01%). This sequence change replaces methionine, which is neutral and non-polar, with arginine, which is basic and polar, at codon 193 of the ACAT1 protein (p.Met193Arg). |
Revvity Omics, |
RCV000844795 | SCV002021694 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2021-04-06 | criteria provided, single submitter | clinical testing | |
Lifecell International Pvt. |
RCV000844795 | SCV003922041 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | criteria provided, single submitter | clinical testing | A Homozygote Missense variant c.578T>G in Exon 6 of the ACAT1 gene that results in the amino acid substitution p.Met193Arg was identified. The observed variant has a minor allele frequency of 0.00001% in gnomAD exomes and genomes, respectively. The severity of the impact of this variant on the protein is high, based on the effect of the protein and REVEL score . Rare Exome Variant Ensemble Learner (REVEL) is an ensembl method for predicting the pathogenicity of missense variants based on a combination of scores from 13 individual tools: MutPred, FATHMM v2.3, VEST 3.0, PolyPhen-2, SIFT, PROVEAN, MutationAssessor, MutationTaster, LRT, GERP++, SiPhy, phyloP, and phastCons. The REVEL score for an individual missense variant can range from 0 to 1, with higher scores reflecting greater likelihood that the variant is disease-causing. ClinVar has also classified this variant as Pathogenic/ LikelyPathogenic(Variant ID 666490). Experimental studies have shown that this missense change affects ACAT1 function (Abdelkreen et al., 2017).This missense change has been observed in individual(s) with beta-ketothiolase deficiency (Abdelkeem et al., 2019). Based on the above evidence this variant has been classified as Pathogenic according to the ACMG guidelines. | |
Natera, |
RCV000844795 | SCV002085829 | pathogenic | Deficiency of acetyl-CoA acetyltransferase | 2020-09-28 | no assertion criteria provided | clinical testing |