Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV004018385 | SCV004848199 | likely pathogenic | Hereditary hemorrhagic telangiectasia | 2018-04-02 | criteria provided, single submitter | clinical testing | The p.Tyr286fs variant in ACVRL1 has not been previously reported in individuals with hereditary hemorrhagic telangiectasia (HHT) and was absent from large population studies. This variant is predicted to cause a frameshift, which alters the protein’s amino acid sequence beginning at position 286 and leads to a premature termination codon 105 amino acids downstream. This alteration is then predicted to lead to a truncated or absent protein. In summary, although additional studies are required to fully establish its clinical significance, the p.Tyr286fs variant is likely pathogenic. ACMG/AMP Criteria applied: PVS1; PM2. |