Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV001581864 | SCV001817985 | pathogenic | not provided | 2019-10-04 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a decrease enzymatic activity of mutant protein when compared with WT protein (Ohba et al., 2013); Not observed in large population cohorts (Lek et al., 2016); In silico analysis, which includes protein predictors and evolutionary conservation, supports a deleterious effect; This variant is associated with the following publications: (PMID: 22983749, 19731322, 28102861) |
Labcorp Genetics |
RCV001581864 | SCV003445387 | pathogenic | not provided | 2023-12-01 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 170 of the ALAS2 protein (p.Arg170Cys). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individuals with X-linked recessive congenital sideroblastic anemia (PMID: 19731322, 22983749, 28102861). This variant is also known as c.397C>T (p.R133C). ClinVar contains an entry for this variant (Variation ID: 1214130). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on ALAS2 protein function. Experimental studies have shown that this missense change affects ALAS2 function (PMID: 22983749). For these reasons, this variant has been classified as Pathogenic. |
Revvity Omics, |
RCV001581864 | SCV003829455 | likely pathogenic | not provided | 2022-09-14 | criteria provided, single submitter | clinical testing |