Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV001756550 | SCV001985455 | uncertain significance | not provided | 2024-08-11 | criteria provided, single submitter | clinical testing | Observed as hemizygous in an asymptomatic male identified by family screening; VLCFA were slightly elevated and D3-C22:0 loading test found that VLCFA metabolism was not significantly impaired supporting that this variant is not associated with X-ALD (PMID: 34946879); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 34946879, 36114283, 24480483, 33690217) |