Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001368455 | SCV001564850 | pathogenic | Adrenoleukodystrophy | 2025-01-20 | criteria provided, single submitter | clinical testing | This variant, c.234_242del, results in the deletion of 3 amino acid(s) of the ABCD1 protein (p.Arg80_Leu82del), but otherwise preserves the integrity of the reading frame. This variant is not present in population databases (gnomAD no frequency). This variant has been observed in individual(s) with X-linked adrenoleukodystrophy (PMID: 10480364; internal data). ClinVar contains an entry for this variant (Variation ID: 1059218). For these reasons, this variant has been classified as Pathogenic. |
Revvity Omics, |
RCV003136041 | SCV003824417 | likely pathogenic | not provided | 2021-12-10 | criteria provided, single submitter | clinical testing | |
Baylor Genetics | RCV001368455 | SCV004204323 | likely pathogenic | Adrenoleukodystrophy | 2023-09-05 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV001368455 | SCV005423465 | likely pathogenic | Adrenoleukodystrophy | 2024-10-03 | criteria provided, single submitter | clinical testing | Variant summary: ABCD1 c.234_242delCCTGCGGCT (p.Arg80_Leu82del) results in an in-frame deletion that is predicted to remove three amino acids from the encoded protein. The variant was absent in 116577 control chromosomes (gnomAD). c.234_242delCCTGCGGCT (also described as del78-80LLR in the literature) has been reported in the literature in individuals affected with adrenoleukodystrophy (examples: Wichers_1999, Matteson_2021). These data indicate that the variant is likely associated with disease. In functional assays, the variant abolished peroxisomal targeting of the protein and resulted in the mislocalization of the protein to nucleus, cytosol and mitochondria (Landgraf_2003). ClinVar contains an entry for this variant (Variation ID: 1059218). The following publications have been ascertained in the context of this evaluation (PMID: 10480364, 33920672, 14533738). Based on the evidence outlined above, the variant was classified as likely pathogenic. |