Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000627370 | SCV000748363 | pathogenic | not provided | 2018-04-13 | criteria provided, single submitter | clinical testing | The Y281X nonsense variant in the ABCD1 gene is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. The Y281X variant is not observed in large population cohorts (Lek et al., 2016). Although this pathogenic variant has not been reported previously to our knowledge, we interpret it to be a pathogenic variant. |
ARUP Laboratories, |
RCV001001992 | SCV001159805 | pathogenic | not specified | 2018-07-03 | criteria provided, single submitter | clinical testing | The ABCD1 c.843C>A; p.Tyr281Ter variant, to our knowledge, is not described in the medical literature but is reported as pathogenic in ClinVar (Variation ID: 523894). It is absent from general population databases (1000 Genomes Project, Exome Variant Server, and Genome Aggregation Database), indicating it is not a common polymorphism. This variant induces an early termination codon and is predicted to result in a truncated protein or mRNA subject to nonsense-mediated decay. Additionally, several downstream truncating variants have been described in association with adrenoleukodystrophy and are considered pathogenic (see link to ALD database and references therein). Based on available information, the p.Tyr281Ter variant is considered pathogenic. References: Link to ALD database: https://adrenoleukodystrophy.info/mutations-and-variants-in-abcd1 |
Genome- |
RCV001800831 | SCV002045816 | likely pathogenic | Adrenoleukodystrophy | 2021-11-07 | criteria provided, single submitter | clinical testing |