Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Baylor Genetics | RCV003466324 | SCV004209936 | likely pathogenic | Mucopolysaccharidosis type 6 | 2023-02-12 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003466324 | SCV004547986 | pathogenic | Mucopolysaccharidosis type 6 | 2023-06-14 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant disrupts a region of the ARSB protein in which other variant(s) (p.Cys521Tyr) have been determined to be pathogenic (PMID: 8116615, 10923267, 24373060). This suggests that this is a clinically significant region of the protein, and that variants that disrupt it are likely to be disease-causing. This variant has not been reported in the literature in individuals affected with ARSB-related conditions. This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Trp438*) in the ARSB gene. While this is not anticipated to result in nonsense mediated decay, it is expected to disrupt the last 96 amino acid(s) of the ARSB protein. |