Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Center for Pediatric Genomic Medicine, |
RCV000224599 | SCV000280768 | pathogenic | not provided | 2015-06-12 | criteria provided, single submitter | clinical testing | |
Laboratory of Diagnosis and Therapy of Lysosomal Disorders, |
RCV000677514 | SCV000803024 | uncertain significance | Mucopolysaccharidosis type 6 | 2018-01-01 | criteria provided, single submitter | curation | Absent from GnomAD (PM2) |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000779750 | SCV000916525 | uncertain significance | not specified | 2018-04-19 | criteria provided, single submitter | clinical testing | Variant summary: ARSB c.215T>A (p.Leu72Gln) results in a non-conservative amino acid change located in the Sulfatase, N-terminal domain (IPR000917) of the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant was absent in 30582 control chromosomes (gnomAD). The available data on variant occurrences in the general population are insufficient to allow any conclusion about variant significance. The variant, c.215T>A, has been reported in the literature in one individual affected with Mucopolysaccharidosis Type VI (Maroteaux-Lamy Syndrome)(Isbrandt_1995), together with the likely pathogenic (in our internal database) variant c.219_230delinsG (p.Asp73fsX50) on the same allele and c.743delC (p.Pro248Leufs*5) on the other allele, suggesting a potential benign effect. The same publication reports experimental evidence evaluating an impact on protein function, however, does not allow convincing conclusions about the variant effect. However, one clinical diagnostic laboratory has submitted clinical-significance assessments for this variant to ClinVar after 2014 without evidence for independent evaluation and classified the variant as pathogenic. In addition, multiple reports in HGMD related to other variants affecting this codon suggest this might be a hotspot. Based on the evidence outlined above, the variant was classified as uncertain significance. |