Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV000193280 | SCV000246680 | pathogenic | Menkes kinky-hair syndrome | 2013-02-08 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000578755 | SCV000680685 | pathogenic | not provided | 2017-11-20 | criteria provided, single submitter | clinical testing | The R795X variant in the ATP7A gene has been previously identified in at least one male with a clinical diagnosis of classical severe Menkes disease (Tümer et al., 1997a; Tümer et al., 1997b). In addition, R795X due to a different nucleotide substitution (c.2383 C>A) has been reported in a 41 year old affected female with skewed inactivation of the X chromosome and a history of intellectual disability, seizures, abnormal hair, slightly increased copper uptake (34 ng) and retention (30.7%), and a family history of classical Menkes disease in a brother who died at 27 months old (Møller et al., 2012). R795X is predicted to cause loss of normal protein function either by protein truncation or nonsense-mediated mRNA decay. Other nonsense variants in the ATP7A gene have been reported in Human Gene Mutation Database in association with Menkes disease (Stenson et al., 2014). Furthermore, the R795X variant is not observed in large population cohorts (Lek et al., 2016). |
Laboratory of Medical Genetics, |
RCV000193280 | SCV001976979 | pathogenic | Menkes kinky-hair syndrome | 2021-10-01 | criteria provided, single submitter | clinical testing | PVS1, PM1, PM2, PP3, PP5 |
Institute for Medical Genetics and Human Genetics, |
RCV000193280 | SCV004037184 | pathogenic | Menkes kinky-hair syndrome | criteria provided, single submitter | not provided | ||
Natera, |
RCV001274025 | SCV001457712 | pathogenic | Menkes kinky-hair syndrome; Cutis laxa, X-linked; X-linked distal spinal muscular atrophy type 3 | 2020-09-16 | no assertion criteria provided | clinical testing | |
Inherited Neuropathy Consortium Ii, |
RCV000193280 | SCV004012044 | uncertain significance | Menkes kinky-hair syndrome | 2016-01-06 | no assertion criteria provided | literature only |