Total submissions: 10
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV004999212 | SCV005620243 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy | 2025-01-09 | reviewed by expert panel | curation | The NM_000070.3: c.2242C>T p.(Arg748Ter) variant in CAPN3, which is also known as p.(Arg748del), is a nonsense variant predicted to cause a premature stop codon in biologically relevant exon 21/24, leading to nonsense mediated decay in a gene in which loss of function is an established disease mechanism. mRNA analysis demonstrated reduced expression of the transcript containing the variant, consistent with nonsense mediated decay (PMID: 17157502) (PVS1). This variant has been detected in at least six individuals reported to have autosomal recessive LGMD (PMID: 25214167, 12461690, 16971480, 17157502, 18055493; Washington University internal clinic data communication). In at least one case, the variant was identified in unknown phase with a pathogenic variant (c.1468C>T p.(Arg490Trp), 0.5 pts, PMID: 16971480), and in at least two cases, the variant was identified in trans with a second CAPN3 variant not yet curated by the VCEP and considered VUS (0.5 pts, PMID: 12461690, 17157502) (PM3). At least one patient with this variant was clinically suspected to have limb girdle muscular dystrophy and displayed reduced calpain-3 protein expression, which is specific for CAPN3-related LGMD (PP4_Moderate; PMID: 16971480). The filtering allele frequency of the variant is 0.000114 for European (non-Finnish) genome alleles in gnomAD v3.1.2 (the upper threshold of the 95% CI of 3/68008), which is more than the LGMD VCEP threshold (<0.0001) for PM2_Supporting (criterion not met). In summary, this variant meets the criteria to be classified as Pathogenic for autosomal recessive limb girdle muscular dystrophy based on the ACMG/AMP criteria applied, as specified by the ClinGen LGMD VCEP (LGMD VCEP specifications version 1.0.0; 01/09/2025): PVS1, PM3, PP4_Moderate. |
Eurofins Ntd Llc |
RCV000725244 | SCV000335247 | pathogenic | not provided | 2018-05-16 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000279441 | SCV000645489 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2025-01-20 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Arg748*) in the CAPN3 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in CAPN3 are known to be pathogenic (PMID: 10330340, 15689361). This variant is present in population databases (rs768090444, gnomAD 0.0009%). This premature translational stop signal has been observed in individuals with autosomal recessive limb-girdle muscular dystrophy (LGMD) (PMID: 12461690, 16971480, 17157502, 18055493). ClinVar contains an entry for this variant (Variation ID: 283259). For these reasons, this variant has been classified as Pathogenic. |
Centre for Mendelian Genomics, |
RCV000279441 | SCV001369821 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2020-03-24 | criteria provided, single submitter | clinical testing | This variant was classified as: Pathogenic. The following ACMG criteria were applied in classifying this variant: PVS1,PM2,PM3,PP4. |
Revvity Omics, |
RCV000725244 | SCV002018067 | pathogenic | not provided | 2019-12-16 | criteria provided, single submitter | clinical testing | |
Athena Diagnostics | RCV000725244 | SCV002770920 | pathogenic | not provided | 2022-08-01 | criteria provided, single submitter | clinical testing | This variant is expected to result in the loss of a functional protein. The frequency of this variant in the general population is consistent with pathogenicity (http://gnomad.broadinstitute.org). In multiple individuals with LGMD, this variant has been seen with a single recessive pathogenic variant in the same gene, suggesting this variant may also be pathogenic. |
Baylor Genetics | RCV003475902 | SCV004211567 | pathogenic | Muscular dystrophy, limb-girdle, autosomal dominant 4 | 2024-03-20 | criteria provided, single submitter | clinical testing | |
Fulgent Genetics, |
RCV005008239 | SCV005637814 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A; Muscular dystrophy, limb-girdle, autosomal dominant 4 | 2024-06-10 | criteria provided, single submitter | clinical testing | |
Counsyl | RCV000279441 | SCV001132143 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2016-12-06 | no assertion criteria provided | clinical testing | |
Natera, |
RCV000279441 | SCV001456372 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2020-09-16 | no assertion criteria provided | clinical testing |