Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000671146 | SCV000796096 | likely pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2017-12-01 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000671146 | SCV001582824 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2020-01-28 | criteria provided, single submitter | clinical testing | Donor and acceptor splice site variants typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in CAPN3 are known to be pathogenic (PMID: 10330340, 15689361). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site, but this prediction has not been confirmed by published transcriptional studies. This variant has been observed in individual(s) with limb girdle muscular dystrophy (PMID: 17994539, 18055493). ClinVar contains an entry for this variant (Variation ID: 555344). This variant is not present in population databases (ExAC no frequency). This sequence change affects a donor splice site in intron 22 of the CAPN3 gene. It is expected to disrupt RNA splicing and likely results in an absent or disrupted protein product. For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV003472135 | SCV004211576 | pathogenic | Muscular dystrophy, limb-girdle, autosomal dominant 4 | 2023-08-23 | flagged submission | clinical testing |