Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV001774552 | SCV002002010 | uncertain significance | not provided | 2020-02-11 | criteria provided, single submitter | clinical testing | Not observed at a significant frequency in large population cohorts (Lek et al., 2016); In silico analysis supports a deleterious effect on splicing; Has not been previously published as pathogenic or benign to our knowledge |
Labcorp Genetics |
RCV002512158 | SCV003486404 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2024-10-16 | criteria provided, single submitter | clinical testing | This sequence change falls in intron 2 of the CAPN3 gene. It does not directly change the encoded amino acid sequence of the CAPN3 protein. RNA analysis indicates that this variant induces altered splicing and may result in an absent or altered protein product. This variant is present in population databases (no rsID available, gnomAD 0.003%). This variant has been observed in individuals with autosomal recessive limb-girdle muscular dystrophy (PMID: 34697879). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 1315302). Studies have shown that this variant alters CAPN3 gene expression (PMID: 34697879). Variants that disrupt the consensus splice site are a relatively common cause of aberrant splicing (PMID: 17576681, 9536098). Studies have shown that this variant results in activation of a cryptic splice site, and produces a non-functional protein and/or introduces a premature termination codon (PMID: 34697879). For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV004571079 | SCV005059993 | pathogenic | Muscular dystrophy, limb-girdle, autosomal dominant 4 | 2024-02-14 | criteria provided, single submitter | clinical testing | |
Rare Diseases Genetics and Genomics, |
RCV002512158 | SCV002822846 | pathogenic | Autosomal recessive limb-girdle muscular dystrophy type 2A | 2021-04-23 | no assertion criteria provided | research |