Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003779404 | SCV004603782 | pathogenic | Congenital myotonia, autosomal recessive form; Congenital myotonia, autosomal dominant form | 2023-12-11 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 17 of the CLCN1 gene. RNA analysis indicates that disruption of this splice site induces altered splicing and likely results in a shortened protein product. This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individuals with autosomal recessive myotonia congenita (PMID: 15116370; Invitae). Studies have shown that disruption of this splice site results in skipping of skipping of exon 17, but is expected to preserve the integrity of the reading-frame (PMID: 15116370). For these reasons, this variant has been classified as Pathogenic. |