Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001389973 | SCV001591535 | pathogenic | Fanconi anemia | 2020-01-31 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Donor and acceptor splice site variants typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in FANCA are known to be pathogenic (PMID: 19367192). Experimental studies have shown that disruption of this splice site affects mRNA splicing (PMID: 24584348). Disruption of this splice site has been observed in individual(s) with Fanconi anemia (PMID: 23067021, 24584348). This variant is not present in population databases (ExAC no frequency). This sequence change affects a donor splice site in intron 28 of the FANCA gene. It is expected to disrupt RNA splicing and likely results in an absent or disrupted protein product. |
Leiden Open Variation Database | RCV001256602 | SCV001426094 | pathogenic | Fanconi anemia complementation group A | 2020-02-28 | no assertion criteria provided | curation | Curator: Arleen D. Auerbach. Submitter to LOVD: Myungshin Kim. |