Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001388440 | SCV001589438 | pathogenic | Fanconi anemia | 2020-05-29 | criteria provided, single submitter | clinical testing | Donor and acceptor splice site variants typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in FANCA are known to be pathogenic (PMID: 19367192). Experimental studies have shown that this variant disrupts mRNA splicing (PMID: 30031030). This variant has been observed in an individual with Fanconi anemia with the variant in trans (on the opposite chromosome) from a pathogenic variant (PMID: 30031030). This variant is not present in population databases (ExAC no frequency). This sequence change affects a donor splice site in intron 8 of the FANCA gene. It is expected to disrupt RNA splicing and likely results in an absent or disrupted protein product. For these reasons, this variant has been classified as Pathogenic. |