Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV004018358 | SCV004848104 | pathogenic | Marfan syndrome | 2019-01-28 | criteria provided, single submitter | clinical testing | The p.Glu375X variant in FBN1 has not been previously reported in individuals with Marfan syndrome or in large population studies. This nonsense variant leads to a premature termination codon at position 375, which is predicted to lead to a truncated or absent protein. Heterozygous loss of function of the FBN1 gene is an established disease mechanism in Marfan syndrome. In summary, this variant meets criteria to be classified as pathogenic for Marfan syndrome in an autosomal dominant manner based upon the predicted impact to the protein and absence in controls. |