Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ambry Genetics | RCV002314299 | SCV000738764 | pathogenic | Familial thoracic aortic aneurysm and aortic dissection | 2016-01-27 | criteria provided, single submitter | clinical testing | The c.4816+1G>T intronic pathogenic mutation results from a G to T substitution one nucleotide downstream of coding exon 38 of the FBN1 gene. This alteration was reported in a cohort of patients with Marfan syndrome who met Ghent criteria (Baetens M et al, Hum. Mutat. 2011 Sep; 32(9):1053-62). In addition to the clinical data presented in the literature, since alterations that disrupt the canonical splice donor site are typically deleterious in nature, this alteration is interpreted as a disease-causing mutation (ACMG Recommendations for Standards for Interpretation and Reporting of Sequence Variations. Revision 2007. Genet Med. 2008;10:294). |
Centre of Medical Genetics, |
RCV000663750 | SCV002025334 | likely pathogenic | Marfan syndrome | 2021-03-01 | criteria provided, single submitter | research | PM2, PS7, PP4 |
Labcorp Genetics |
RCV002531817 | SCV003442878 | pathogenic | Marfan syndrome; Familial thoracic aortic aneurysm and aortic dissection | 2022-01-04 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 39 of the FBN1 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in FBN1 are known to be pathogenic (PMID: 17657824, 19293843). This variant is not present in population databases (gnomAD no frequency). For these reasons, this variant has been classified as Pathogenic. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. ClinVar contains an entry for this variant (Variation ID: 519695). Disruption of this splice site has been observed in individuals with FBN1-related conditions (PMID: 21542060, 31471346). |
Center for Medical Genetics Ghent, |
RCV000663750 | SCV000787094 | likely pathogenic | Marfan syndrome | 2017-11-07 | no assertion criteria provided | clinical testing |