Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV000035218 | SCV000058863 | likely pathogenic | Marfan syndrome | 2012-04-17 | criteria provided, single submitter | clinical testing | The Cys166Ser variant (FBN1) has been reported in one individual with clinical f eatures of Marfan syndrome (Biggin 2004). In addition, functional analysis revea ls that the variant affects normal fibrillin microfibril assembly (Massan-Wu 201 0). Furthermore, this variant alters a conserved cysteine residue which is predi cted to disrupt a disulfide bridge in an EGF-like domain of the protein. Cystein e residue alterations in EGF-like domains of FBN1 are commonly altered in patien ts with clinical features of Marfan syndrome (Schrijver 1999). In summary, this variant is likely to be pathogenic, though segregation studies and functional an alyses are required to fully establish the pathogenicity of this variant. |