Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Petrovsky National Research Centre of Surgery, |
RCV000851489 | SCV000930691 | likely pathogenic | Marfan syndrome | 2019-08-01 | criteria provided, single submitter | clinical testing | The c.5329T>C(p.Cys1777Arg) variant is absent in large population studies. There is a known other AA substitution (p.Cys1777Tyr) but at a next position (c.5330G>A), which has been reported in ClinVar (rs1060501069, Variation ID:406341) with a well-established evidences on Likely pathogenic classification of amino acid substitution. Cysteine is located in very conservative residue of EGF-like domain of Fibrillin-1. Alterations in such domains result in mutation with high disease-cause chances (DOI:10.1002/humu.1380010504). Additionally, computational results of NetGene2, Provean, SIFT, PolyPhen2 for Cys1777Arg show damaging effect. Based on this evidences we evaluate c.5329T>C/N (p.Cys1777Arg) as likely pathogenic. Functional study deemed necessary. |