Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Blueprint Genetics | RCV000208432 | SCV000263916 | likely pathogenic | Marfan syndrome | 2015-11-27 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000532804 | SCV000627946 | pathogenic | Marfan syndrome; Familial thoracic aortic aneurysm and aortic dissection | 2025-01-25 | criteria provided, single submitter | clinical testing | This sequence change affects an acceptor splice site in intron 48 of the FBN1 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in FBN1 are known to be pathogenic (PMID: 17657824, 19293843). This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individuals with clinical features of FBN1-related conditions (PMID: 16220557, 20564469; internal data). ClinVar contains an entry for this variant (Variation ID: 222617). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Ambry Genetics | RCV002354586 | SCV002653340 | likely pathogenic | Familial thoracic aortic aneurysm and aortic dissection | 2019-08-09 | criteria provided, single submitter | clinical testing | The c.5918-2A>G intronic variant results from an A to G substitution two nucleotides upstream from coding exon 48 in the FBN1 gene. This nucleotide position is highly conserved in available vertebrate species. Using the BDGP and ESEfinder splice site prediction tools, this alteration is predicted to abolish the native splice acceptor site; however, direct evidence is unavailable. Alterations that disrupt the canonical splice site are expected to cause aberrant splicing, resulting in an abnormal protein or a transcript that is subject to nonsense-mediated mRNA decay. As such, this alteration is classified as likely pathogenic. |
Clinical Genetics Laboratory, |
RCV004696873 | SCV005197873 | likely pathogenic | not provided | 2022-07-07 | criteria provided, single submitter | clinical testing |