Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV001756598 | SCV001986081 | uncertain significance | not provided | 2021-04-19 | criteria provided, single submitter | clinical testing | Not observed in large population cohorts (Lek et al., 2016); Located at the intronic +5 splice site; however, the natural splice donor site of intron 63 is not predicted by in-silico analysis. In the absence of RNA/functional studies, the actual effect of this sequence change is unknown; This variant is associated with the following publications: (PMID: 25525159, 9401003, 18435798) |
Department of Laboratory Medicine and Genetics, |
RCV005050402 | SCV005684936 | likely pathogenic | Marfan syndrome | 2025-01-02 | no assertion criteria provided | clinical testing | The NM_000138.5:c.7819+5G>A is considered to be rare in the general population database (gnomAD v2.1.1). This variant is predicted to be deleterious by in-silico analysis (SpliceAI). This variant was found in a patient with Marfan syndrome (PMID: 9401003; 18435798). This variant was found in a patient with Marfan syndrome meeting revised Ghent criteria (aortic root dilatation and a systemic score of 9 points) (Samsung Medical Center internal data). According to the ClinGen guidance for PP1/BS4 and PP4 criteria (PMID: 38103548), PP4 with weighted strength was applied. In summary, this variant was classified as a likely pathogenic variant for Marfan syndrome (PP3, PP4 with weighted strength, PS4_P, PM2_P). |