Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001386359 | SCV001586550 | pathogenic | Glycogen storage disease, type II | 2020-03-30 | criteria provided, single submitter | clinical testing | This variant is not present in population databases (ExAC no frequency). For these reasons, this variant has been classified as Pathogenic. Loss-of-function variants in GAA are known to be pathogenic (PMID: 18425781, 22252923). A different variant (c.1442G>A) giving rise to the same protein effect observed here (p.Trp481*) has been determined to be pathogenic (PMID: 22252923). This suggests that this variant is also likely to be causative of disease. This variant has not been reported in the literature in individuals with GAA-related conditions. This sequence change creates a premature translational stop signal (p.Trp481*) in the GAA gene. It is expected to result in an absent or disrupted protein product. |
Arcensus | RCV001386359 | SCV002564605 | pathogenic | Glycogen storage disease, type II | 2013-02-01 | criteria provided, single submitter | clinical testing |