Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001960734 | SCV002235071 | pathogenic | Glycogen storage disease, type II | 2021-05-31 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Studies have shown that this variant is associated with incorrect splicing, which introduces a premature termination codon or an in-frame deletion (PMID: 22676651). This variant has been observed in individual(s) with Pompe disease (PMID: 22676651). This variant is not present in population databases (ExAC no frequency). This sequence change affects an acceptor splice site in intron 11 of the GAA gene. RNA analysis indicates that this variant induces altered splicing and may result in an absent or disrupted protein product. |