Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000631054 | SCV000752043 | uncertain significance | Glycogen storage disease, type II | 2017-10-17 | criteria provided, single submitter | clinical testing | This sequence change replaces glycine with aspartic acid at codon 576 of the GAA protein (p.Gly576Asp). The glycine residue is highly conserved and there is a moderate physicochemical difference between glycine and aspartic acid. This variant is not present in population databases (ExAC no frequency). This variant has been reported in an individual affected with Pompe disease (PMID: 18425781). Experimental studies have shown that this missense leads to sub celular mislocalization of the GAA protein and its loss of enzymatic activity (PMID: 18425781). In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |