Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Therapies Laboratory, |
RCV001078140 | SCV001156138 | pathogenic | Glycogen storage disease, type II | no assertion criteria provided | clinical testing | Low GAA enzyme activity (<0.1 units); urine tetrasaccharides elevated (150 units); respiratory functions normal |