Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Revvity Omics, |
RCV001783338 | SCV002023869 | pathogenic | not provided | 2020-04-04 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003502608 | SCV004297575 | pathogenic | Glycogen storage disease, type II | 2023-08-28 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Cys103*) in the GAA gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in GAA are known to be pathogenic (PMID: 18425781, 22252923). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with clinical features of Pompe disease (PMID: 14695532). ClinVar contains an entry for this variant (Variation ID: 1322963). For these reasons, this variant has been classified as Pathogenic. |