Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Broad Center for Mendelian Genomics, |
RCV001829301 | SCV002097086 | uncertain significance | Glycogen storage disease, type IV | 2022-01-27 | criteria provided, single submitter | curation | The p.Arg565Gln variant in GBE1 has been reported in 1 compound heterozygous individual with adult polyglucosan body disease (APBD) (PMID: 23034915) and has been identified in 0.01% (3/22110) of African/African American chromosomes by the Genome Aggregation Database (gnomAD, http://gnomad.broadinstitute.org; dbSNP ID: rs774619760). Although this variant has been seen in the general population in a heterozygous state, its frequency is not high enough to rule out a pathogenic role. Computational prediction tools and conservation analyses suggest that this variant may impact the protein, though this information is not predictive enough to determine pathogenicity. In summary, the clinical significance of the p.Arg565Gln variant is uncertain. ACMG/AMP Criteria applied: PP3, PM3_supporting (Richards 2015). |
Baylor Genetics | RCV001829301 | SCV004198697 | pathogenic | Glycogen storage disease, type IV | 2024-03-28 | criteria provided, single submitter | clinical testing |