Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003313358 | SCV004012131 | pathogenic | Monogenic diabetes | 2023-06-24 | reviewed by expert panel | curation | The c.1343del variant in the glucokinase gene, GCK, causes a frameshift in the protein at codon 448 (NM_000162.5), adding 166 novel amino acids before encountering a stop codon (p.(Gly448AlafsTer166)). This variant, located in exon 10 of 10, is predicted to cause loss of a stop codon and result in an elongated protein. The additional residues are expected to cause improper folding, resulting in loss of function in a gene in which loss-of-function is an established disease mechanism (PVS1; PMID 19790256). Additionally, this variant is absent from gnomAD v2.1.1 (PM2_Supporting). This variant was identified in an individual with a clinical history highly specific for GCK-MODY (FBG 5.5-8 mmol/L and HbA1c 5.6 - 7.6%, negative antibodies, and a three generation family history of diabetes) (PP4_Moderate; internal lab contributor). In summary, the c.1343del variant meets the criteria to be classified as pathogenic for monogenic diabetes. ACMG/AMP criteria applied, as specified by the ClinGen MDEP (specification version 1.2.0, approved 6/7/2023): PVS1, PP4_Moderate, PM2_Supporting). |