Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ambry Genetics | RCV002338076 | SCV002639197 | pathogenic | Maturity onset diabetes mellitus in young | 2016-09-20 | criteria provided, single submitter | clinical testing | The c.483+1G>A intronic pathogenic mutation results from a G to A substitution one nucleotide after coding exon 4 of the GCK gene. This variant was detected in one individual with maturity-onset diabetes of the young (MODY) as well as four individuals from one family from a population that was described as hyperglycemic (Osbak KK et al. Hum. Mutat., 2009 Nov;30:1512-26; Steele AM et al. JAMA, 2014 Jan;311:279-86). In addition to the clinical data presented in the literature, alterations that disrupt the canonical splice site are expected to cause aberrant splicing, resulting in an abnormal protein or a transcript that is subject to nonsense-mediated mRNA decay. As such, this alteration is interpreted as a disease-causing mutation. |