Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000197033 | SCV000253768 | pathogenic | Charcot-Marie-Tooth Neuropathy X | 2023-11-30 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 183 of the GJB1 protein (p.Arg183Cys). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individuals with Charcot-Marie-Tooth disease (PMID: 9187667, 11271367, 25429913, 28469099). ClinVar contains an entry for this variant (Variation ID: 216039). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt GJB1 protein function with a positive predictive value of 80%. Experimental studies have shown that this missense change affects GJB1 function (PMID: 1211842, 27844031). This variant disrupts the p.Arg183 amino acid residue in GJB1. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 9187667, 12111842, 15719046, 27027447, 27844031). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV000235360 | SCV000293450 | pathogenic | not provided | 2021-10-29 | criteria provided, single submitter | clinical testing | Reported previously in association with CMTX in affected males and females (Bone et al., 1997, Hahn et al., 2001, Bort et al., 1997); Not observed at significant frequency in large population cohorts (Lek et al., 2016); Missense variants in this gene are often considered pathogenic (Stenson et al., 2014); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 24444136, 21871435, 9361298, 11271367, 12111842, 25429913, 12457340, 9187667, 31211173, 32376792, 34060689, 32903794, 30952033, 30042657) |
Athena Diagnostics | RCV000235360 | SCV000613490 | likely pathogenic | not provided | 2017-12-29 | criteria provided, single submitter | clinical testing | |
Neuro |
RCV000754745 | SCV000882635 | likely pathogenic | Charcot-Marie-Tooth disease X-linked dominant 1 | 2018-10-08 | criteria provided, single submitter | clinical testing | |
Mayo Clinic Laboratories, |
RCV000235360 | SCV004226251 | pathogenic | not provided | 2022-10-14 | criteria provided, single submitter | clinical testing | PP3, PM1, PM2, PS3, PS4 |
Inherited Neuropathy Consortium | RCV000789836 | SCV000929220 | uncertain significance | Charcot-Marie-Tooth disease | no assertion criteria provided | literature only |