Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Invitae | RCV000530926 | SCV000622188 | pathogenic | Fabry disease | 2017-03-06 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. While this particular variant has not been reported in the literature, loss-of-function variants in GLA are known to be pathogenic (PMID: 10666480, 12175777). This sequence change deletes 5 nucleotides from exon 1 of the GLA mRNA (c.50_54delGCTTC), causing a frameshift at codon 17. This creates a premature translational stop signal (p.Arg17Profs*12) and is expected to result in an absent or disrupted protein product. |