Total submissions: 8
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Eurofins Ntd Llc |
RCV000179267 | SCV000231489 | pathogenic | not provided | 2015-11-23 | criteria provided, single submitter | clinical testing | |
Color Diagnostics, |
RCV001185735 | SCV001352002 | likely pathogenic | Fabry disease | 2022-08-31 | criteria provided, single submitter | clinical testing | This missense variant replaces methionine with valine at codon 296 of the GLA protein. Computational prediction suggests that this variant may have deleterious impact on protein structure and function (internally defined REVEL score threshold >= 0.7, PMID: 27666373). An experimental study has shown that this variant leads to 11-12% residual GLA enzyme activity when expressed in COS-7 cells (PMID: 17555407). This variant has been reported in an adult male affected with mild cardiac variant of Fabry disease (PMID: 1846223). Residual GLA enzyme activity was detectable in cells from this patient. This variant has been reported in individuals affected with Fabry disease with symptoms confined to the kidney (PMID: 29204651, 30890379, 31798221; doi:10.1016/j.ymgme.2016.11.104; doi: 10.5812/numonthly.105759). A different missense variant occurring at the same codon, p.Met296Ile (Clinvar variation ID 10763), has been reported in multiple Japanese males affected with mild, late-onset Fabry disease (PMID: 7596372, 30386727), indicating that methionine at this position is important for GLA protein function. This variant has not been identified in the general population by the Genome Aggregation Database (gnomAD). Based on the available evidence, this variant is classified as Likely Pathogenic. |
Baylor Genetics | RCV001185735 | SCV001522948 | pathogenic | Fabry disease | 2020-11-05 | criteria provided, single submitter | clinical testing | This variant was determined to be pathogenic according to ACMG Guidelines, 2015 [PMID:25741868]. |
Genome- |
RCV001185735 | SCV002054395 | likely pathogenic | Fabry disease | 2021-07-15 | criteria provided, single submitter | clinical testing | |
Fulgent Genetics, |
RCV001185735 | SCV002784805 | likely pathogenic | Fabry disease | 2021-07-13 | criteria provided, single submitter | clinical testing | |
Revvity Omics, |
RCV000179267 | SCV003826327 | pathogenic | not provided | 2022-11-17 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000179267 | SCV005201464 | pathogenic | not provided | 2023-11-13 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate reduced alpha-galactosidase activity (PMID: 17555407, 21598360); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 21598360, 1846223, 24386359, 25382311, 17555407, 29204651, 26833297, 27535533, 20031620, 20108436, 28615118, 27560961) |
OMIM | RCV000011464 | SCV000031696 | pathogenic | Fabry disease, cardiac variant | 1991-02-07 | no assertion criteria provided | literature only |