Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Women's Health and Genetics/Laboratory Corporation of America, |
RCV004586260 | SCV005077081 | pathogenic | Bernard Soulier syndrome | 2024-04-22 | criteria provided, single submitter | clinical testing | Variant summary: GP1BA c.376A>G (p.Asn126Asp) results in a conservative amino acid change in the encoded protein sequence. Four of five in-silico tools predict a damaging effect of the variant on protein function. The variant was absent in 249218 control chromosomes (gnomAD). c.376A>G has been reported in the literature in individuals affected with Bernard Soulier Syndrome (e.g. Savoia_2011, Vettore_2011). These data indicate that the variant is likely to be associated with disease. At least one publication reports experimental evidence evaluating an impact on protein expression in patient cells, finding a loss of GP1BA protein and mRNA expression, as well as a loss of GP1BB protein (Vettore_2011). The following publications have been ascertained in the context of this evaluation (PMID: 21173099, 21993687). No submitters have cited clinical-significance assessments for this variant to ClinVar. Based on the evidence outlined above, the variant was classified as pathogenic. |