Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000807669 | SCV000947735 | pathogenic | not provided | 2021-10-10 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant disrupts the C-terminus of the HMBS protein. Other variant(s) that disrupt this region (p.Gln328Valfs*30, p.Leu329Phefs*30, p.Gly335Alafs*9, and p.Arg355Profs*4) have been observed in individuals with HMBS-related conditions (PMID: 8168829, 9463797, 9702975, 10944860, 19138865). This suggests that this may be a clinically significant region of the protein. ClinVar contains an entry for this variant (Variation ID: 652166). This premature translational stop signal has been observed in individuals with acute intermittent porphyria (PMID: 10782018, 11831862). This variant is not present in population databases (ExAC no frequency). This sequence change creates a premature translational stop signal (p.Gln292*) in the HMBS gene. While this is not anticipated to result in nonsense mediated decay, it is expected to disrupt the last 70 amino acid(s) of the HMBS protein. |
3billion | RCV003152735 | SCV003841666 | likely pathogenic | Acute intermittent porphyria | 2023-02-23 | criteria provided, single submitter | clinical testing | The variant is not observed in the gnomAD v2.1.1 dataset. This variant was predicted to result in a loss or disruption of normal protein function through protein truncation. The predicted truncated protein may be shortened by more than 10%. The variant has been reported to be associated with HMBS related disorder (ClinVar ID: VCV000652166 / PMID: 10782018). Therefore, this variant is classified as Likely pathogenic according to the recommendation of ACMG/AMP guideline. |
Center for Genomic Medicine, |
RCV003152735 | SCV004807840 | likely pathogenic | Acute intermittent porphyria | 2024-03-29 | criteria provided, single submitter | clinical testing |