Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Neuberg Centre For Genomic Medicine, |
RCV001375841 | SCV004048019 | uncertain significance | Mucopolysaccharidosis, MPS-II | criteria provided, single submitter | clinical testing | The inframe deletion variant p.R4Q in LIPA (NM_000235.4) in IDS gene has been submitted to ClinVar as Likely Pathogenic, but no details are available for independent assessment. It has not been reported in affected individuals. The p.Leu41del variant is novel (not in any individuals) in gnomAD Exomes and 1000 Genomes. This p.Leu41del causes deletion of amino acid Leucine at position 41. Since this inframe deletion/insertion is not expected to cause protein truncation, the above variant has been classified as Variant of Uncertain Significance (VUS). | |
Laboratory of Diagnosis and Therapy of Lysosomal Disorders, |
RCV001375841 | SCV005089166 | pathogenic | Mucopolysaccharidosis, MPS-II | 2024-06-07 | criteria provided, single submitter | literature only | Prevalence of the variant significantly increased in affected individuals compared with controls (PS4_Moderate), Absent from controls (or at low frequency) in gnomAD database (PM2_Moderate), Protein length changes in a nonrepeat region or stop–loss variants (PM4_Strong), Multiple lines of computational evidence support a deleterious effect (PP3_Supporting), Patient’s phenotype or family history highly specific for the disease (PP4_Moderate) |
Pediatrics, |
RCV001375841 | SCV001572613 | likely pathogenic | Mucopolysaccharidosis, MPS-II | 2014-05-01 | no assertion criteria provided | research | The variant c.121_123delCTC (p.L41del) was found to be a small in-frame deletion, where the peptide sequence gets shortened by an aliphatic nonpolar neutral amino acid, Leucine at 41 position. It was detected in the hemizygous condition in one of the patients with sever MPS-2 phenotype from Uttarpradesh state of India. |