Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Revvity Omics, |
RCV003146149 | SCV003829500 | likely pathogenic | Mucopolysaccharidosis, MPS-II | 2022-03-17 | criteria provided, single submitter | clinical testing | |
Prevention |
RCV003420582 | SCV004108362 | likely pathogenic | IDS-related disorder | 2023-06-16 | criteria provided, single submitter | clinical testing | The IDS c.353C>T variant is predicted to result in the amino acid substitution p.Thr118Ile. This variant was reported in an individual with Mucopolysaccharidosis II, severe phenotype (Froissart et al. 1998. PubMed ID: 9660053) and in another individual with Mucopolysaccharidosis II, mild phenotype (Villani et al. 2000. PubMed ID: 10838181). In vitro expression studies in COS7 cells show that this variant results in significantly decreased enzymatic activity, 6.7% of wild type (Villani et al. 2000. PubMed ID: 10838181). This variant has not been reported in a large population database (http://gnomad.broadinstitute.org), indicating this variant is rare. This variant is interpreted as likely pathogenic. |
Laboratory of Diagnosis and Therapy of Lysosomal Disorders, |
RCV003146149 | SCV005089001 | pathogenic | Mucopolysaccharidosis, MPS-II | 2024-06-07 | criteria provided, single submitter | literature only | De novo (PS2_Moderate), Absent from controls (or at low frequency) in gnomAD database (PM2_Moderate), Missense variant in a gene with a low rate of benign missense variation (PP2_Supporting), Multiple lines of computational evidence support a deleterious effect (PP3_Supporting), Patient’s phenotype or family history highly specific for the disease (PP4_Strong) |