Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000674066 | SCV000799339 | likely pathogenic | Hurler syndrome | 2018-04-13 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000807531 | SCV000947588 | pathogenic | Mucopolysaccharidosis type 1 | 2022-05-25 | criteria provided, single submitter | clinical testing | This sequence change replaces asparagine, which is neutral and polar, with lysine, which is basic and polar, at codon 348 of the IDUA protein (p.Asn348Lys). This variant is present in population databases (rs746766617, gnomAD 0.0009%). This missense change has been observed in individual(s) with IDUA-related conditions (PMID: 21394825, 23837464, 24875751). ClinVar contains an entry for this variant (Variation ID: 557870). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt IDUA protein function. Experimental studies have shown that this missense change affects IDUA function (PMID: 24875751). For these reasons, this variant has been classified as Pathogenic. |
Revvity Omics, |
RCV001784290 | SCV002023087 | pathogenic | not provided | 2021-09-03 | criteria provided, single submitter | clinical testing |