Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003222578 | SCV003916006 | uncertain significance | Glanzmann thrombasthenia | 2023-04-06 | reviewed by expert panel | curation | The NM_000212.3(ITGB3):c.2T>C (p.Met1Thr) may cause a truncated or absent protein by altering the start codon of the coding sequence and is predicted to lead to the omission of a critical region of the protein. At least one variant (c.31T>C; p.Trp11Arg) has been classified Pathogenic upstream of the next potential in-frame start codon at residue 48 (PVS1_Moderate). Patient 1, of PMID: 31029159, is reported to have a clinical diagnosis of GT and is homozygous for this variant (PM3_supporting). This variant is absent from gnomAD v2.1.1 (PM2_Supporting). In summary, this variant meets the criteria to be classified as uncertain significance for autosomal recessive Glanzmann Thrombasthenia based on the ACMG/AMP criteria applied, as specified by the ClinGen PD VCEP: PVS1_moderate, PM2_supporting, PM3_supporting (VCEP specifications version 2.1). |