Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000851823 | SCV003915995 | pathogenic | Glanzmann thrombasthenia | 2023-03-21 | reviewed by expert panel | curation | NM_000212.3(ITGB3):c.55dup (p.Ala19GlyfsTer?) is a frameshift variant in exon 1 predicted to cause a premature stop codon in biologically-relevant-exon 2/15 and is predicted to lead to nonsense mediated decay in a gene in which loss-of-function is an established mechanism (PVS1). This variant is absent from gnomAD v2.1.1 (PM2_Supporting). Patient TGP0454, PMID:31064749, is reported to have a clinical diagnosis of GT type 1 and is homozygous for this variant (PM3_supporting). In summary, this variant meets the criteria to be classified as Pathogenic for autosomal recessive Glanzmann Thrombasthenia based on the ACMG/AMP criteria applied, as specified by the ClinGen PD VCEP: PVS1, PM2_supporting, PM3_supporting (VCEP specifications version 2.1). |
NIHR Bioresource Rare Diseases, |
RCV000851823 | SCV000899807 | likely pathogenic | Glanzmann thrombasthenia | 2019-02-01 | criteria provided, single submitter | research |