Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV000146374 | SCV000193658 | pathogenic | Severe X-linked myotubular myopathy | 2013-02-08 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000579109 | SCV000680686 | pathogenic | not provided | 2017-11-02 | criteria provided, single submitter | clinical testing | The R37X variant in the MTM1 gene has been reported previously in multiple patients with X-linked myotubular myopathy (Laporte et al., 1997; Buj-Bello et al., 1999; Herman et al., 2002). This variant is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. The R37X variant is not observed in large population cohorts (Lek et al., 2016). We interpret R37X as a pathogenic variant. |
Labcorp Genetics |
RCV000146374 | SCV002180146 | pathogenic | Severe X-linked myotubular myopathy | 2023-07-13 | criteria provided, single submitter | clinical testing | This premature translational stop signal has been observed in individual(s) with myotubular myopathy (PMID: 9305655, 28685322). In at least one individual the variant was observed to be de novo. This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Arg37*) in the MTM1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in MTM1 are known to be pathogenic (PMID: 9305655, 10063835). ClinVar contains an entry for this variant (Variation ID: 158895). For these reasons, this variant has been classified as Pathogenic. |