Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV000146376 | SCV000193660 | pathogenic | Severe X-linked myotubular myopathy | 2013-02-08 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000146376 | SCV001404208 | pathogenic | Severe X-linked myotubular myopathy | 2019-10-25 | criteria provided, single submitter | clinical testing | This variant is not present in population databases (ExAC no frequency). This variant has been observed in individual(s) with myotubular myopathy (PMID: 8640223, 12031625, 10714588, 28685322). In at least one individual the variant was observed to be de novo. This variant is also known as G1186A, G396R in the literature. ClinVar contains an entry for this variant (Variation ID: 158897). This variant has been reported to affect MTM1 protein function (PMID: 10900271, 12118066). For these reasons, this variant has been classified as Pathogenic. This sequence change replaces glycine with arginine at codon 378 of the MTM1 protein (p.Gly378Arg). The glycine residue is highly conserved and there is a moderate physicochemical difference between glycine and arginine. |
Ambry Genetics | RCV001266066 | SCV001444238 | likely pathogenic | Inborn genetic diseases | 2018-04-10 | criteria provided, single submitter | clinical testing | |
3billion | RCV000146376 | SCV005903848 | pathogenic | Severe X-linked myotubular myopathy | 2023-12-08 | criteria provided, single submitter | clinical testing | The variant is not observed in the gnomAD v2.1.1 dataset. Predicted Consequence/Location: Missense variant In silico tool predictions suggest damaging effect of the variant on gene or gene product [REVEL: 0.94 (>=0.6, sensitivity 0.68 and specificity 0.92); 3Cnet: 0.97 (>=0.6, sensitivity 0.72 and precision 0.9)]. Same nucleotide change resulting in same amino acid change has been previously reported as pathogenic/likely pathogenic with strong evidence (ClinVar ID: VCV000158897 /PMID: 8640223). The variant has been observed in multiple (>3) similarly affected unrelated individuals (PMID: 10714588, 12031625, 28685322, 8640223). Different missense changes at the same codon (p.Gly378Glu, p.Gly378Val) have been reported to be associated with MTM1 related disorder (ClinVar ID: VCV001028156 /PMID: 10063835). Therefore, this variant is classified as Pathogenic according to the recommendation of ACMG/AMP guideline. |