Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000521357 | SCV000617412 | pathogenic | not provided | 2023-03-13 | criteria provided, single submitter | clinical testing | Also known as c.191-11T>A; Reported in a female patient with mild clinical features of myotubular myopathy and skewed X-inactivation (Flex et al., 2002); Non-canonical splice site variant demonstrated to result in loss of function (Tanner et al., 1999); Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 25525159, 10790201, 12031625, 10063835) |